Orphan Drugs: In Development

"Orphan Drugs in Development" is presented by the Pharmaceutical Manufacturers Association in cooperation
with the following organizations:

Alpha Kappa Alpha Sorority, Inc.
American Academy of Ophthalmology
American Council for Drug Education
American Foundation for AIDS Research (AmFAR)
American Porphyria Foundation
Asthma & Allergy Foundation of America
Benign Essential Blepharospasm Research Foundation
Chronic Granulomatous Disease Association
Cornelia de Lange Syndrome Foundation
Cystic Fibrosis Foundation
Delta Sigma Theta Sorority
Dystrophic Epidermolysis Bullosa Research
Association (D.E.B.R.A.)
Ehlers-Danlos National Foundation
Epilepsy Foundation of America
Food and Drug Administration, Office of Orphan
Products Development
Guillain-Barre Syndrome Foundation International
Immune Deficiency Foundation
Infectious Diseases Society of America
International Rett Syndrome Association
Leukemia Society of America
Metabolic Information Network
Muscular Dystrophy Association
Narcolepsy & Cataplexy Foundation of America
National Alopecia Areata Foundation
National Black Child Development Institute
National Black Nurses' Association, Inc.

National Cancer Institute
National Center for Nursing Research
National Center for Research Resources
National Coalition of Hispanic Health and Human
Services Organizations (COSSMHO)
National Gaucher's Foundation
National Heart, Lung and Blood Institute
National Institute of Allergy and Infectious Diseases
National Institute of Arthritis and Musculoskeletal
and Skin Diseases
National Institute of Child Health and Human
Development
National Institute of Dental Research
National Institute of Diabetes and Digestive and
Kidney Diseases
National Institute of General Medical Sciences
National Institute of Neurological Disorders and
Stroke
National Institute on Aging
National MPS Society, Inc.
National Multiple Sclerosis Society
National Organization for Rare Disorders, Inc.
National Society to Prevent Blindness, Inc.
Pediatric AIDS Foundation
Sjogren's Syndrome Foundation, Inc.
Society for Pediatric Dermatology
Tourette Syndrome Association

Being listed in this report in no way implies that the above-mentioned organizations endorse or recommend
the use of any of the products in development contained in this publication. For further information, patients
should consult their physicians.

Pharmaceutical
Manufacturers
Association
America's Pharmaceutical Research Companies
1100 15th Street, NW Washington, DC 20005 *Telephone [phone] III11111 iiiiiiiiiilllliiiiiiiiiiiillll
5571095.0504.010

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